A new study shows that the front and back parts of the brain actually develop completely independently of each other.

As someone living with SMA, columnist Halsey Blocher says her physical state has never quite matched her numerical age.

When columnist Jasmine Ramos was born, there was no treatment for SMA. But scientific advances have changed the trajectory of ...

Columnist Connie Chandler's school days were unremarkable, thanks to the kindness of friends and the special accommodations ...

Researchers at Cedars-Sinai are working on a potential stem cell treatment for three siblings in California with an ultra ...

Children with SMA already experiencing symptoms showed gains in motor abilities after receiving gene therapy, a real-world ...

Columnist Kevin Schaefer celebrates the approval of Isembyld for SMA, and remembers the relentless enthusiasm of his friend ...

Columnist Ari Anderson has learned to use his time wisely so that he can enjoy fun activities while also completing the work ...

Keynote speaker Mindy Henderson redefines "impossible" ahead of MDA Engage: Chicago, taking place Sept. 25-26 at the Westin ...

Columnist Brianna Albers used to trust her doctors completely, but having a rare disease forced her to recognize they don't know everything.

The muscle-strengthening agent apitegromab, now Isembyld, has been approved in the U.S. as an add-on treatment for spinal muscular atrophy.