News

Vinay Prasad returns to US' FDA, resumes role overseeing vaccine, gene therapy, STAT News reports
Vinay Prasad is returning to his role at the U.S. Food and Drug Administration to resume overseeing vaccine, gene therapy and ...
Vinay Prasad returns to US' FDA, resumes role overseeing vaccine, gene therapy
Vinay Prasad is returning to his role at the U.S. Food and Drug Administration, a little more than a week after he had left ...
MedPage Today on MSN1d
FDA Restricts Gene Therapy Skysona Due to Blood Cancer Risk
The FDA approved labeling changes for elivaldogene autotemcel (eli-cel; Skysona), a one-time gene therapy for patients with ...
Fierce Pharma1d
FDA restricts bluebird bio gene therapy Skysona after blood cancer reports
After telegraphing an investigation in November, the FDA has moved to restrict the use of bluebird bio’s gene therapy Skysona ...
GEN - Genetic Engineering and Biotechnology News7d
Gene Therapy Companies Set Sights on Cardiovascular Disease
The primary safety risks associated with gene therapy include immune reactions and off-target effects in unintended organs, ...
FDA Chief Says He Wants Gene Therapy Head Prasad to Return
US Food and Drug Administration Commissioner Marty Makary said he’s trying to persuade Vinay Prasad, the agency’s former head ...
FDA’s Reversal on Gene Therapy Helps My Son
Parents of boys with Duchenne muscular dystrophy weigh in on drug innovation and medical regulation.
The American Journal of Managed Care8d
Progress and Challenges With Gene Therapy in Hereditary Hearing Loss
Gene therapy appears to be a promising approach for a subset of genetic deafness, although challenges remain with development ...
EurekAlert!3d
Breakthrough gene therapy for neovascular age-related macular degeneration shows promise in animal models and patients
A groundbreaking study titled "An Engineered Intravitreal Injection Retinal-Pigment-Epithelium-Tropic Adeno-Associated Virus ...
X-SCID gene therapy gives scientists a rare glimpse into early immune system
Findings from St. Jude Children's Research Hospital demonstrate that virtual memory T cells, a specialized group of immune ...
Sarepta reportedly hired Trump-linked lobbying firm after gene therapy deaths
Sarepta Therapeutics (SRPT) stock in focus as report says company hired a Trump-linked lobbying firm after deaths linked to ...
Two boys died after a gene therapy. This family won’t give up hope.
The Revell family hoped a gene therapy could buy time for their sons, who have a rare and fatal disease. After two patients ...