A fundraising campaign for 23-month-old Vedansh Singh, who has SMA Type 1, has received a major boost after influencer Mayuresh Gujar claimed Anant Ambani offered to cover his ₹9 crore treatment cost, ...

BioMarin shared five-year data showing a combination therapy helped adults with late-onset Pompe disease maintain motor function.

Jeae Orthopedic Clinic said on the 2nd that it will apply a minimally invasive technique using a mini arthroscope ...

A reader with a family history of OPMD asks if testosterone therapy can help with fatigue and muscle weakness.