STAAR study demonstrated positive mean annualized estimated glomerular filtration rate (eGFR) slope at 52-weeks across all dosed patients in the ...

Important Safety Information Indication Elfabrio ® (pegunigalsidase alfa for injection) is an enzyme replacement therapy indicated for the longterm treatment of adult patients with a confirmed ...

Therapeutics has initiated a rolling submission of a BLA to the FDA seeking accelerated approval of isaralgagene civaparvovec, or ST-920, a wholly owned investigational gene therapy for the treatment ...

Kidney organoids designed with the same mutation as that present in Fabry disease can help investigators better understand how the disease functions, authors suggested. A new report makes the case ...

Most patients with Fabry disease reported decreased physical and mental health-related quality of life (HRQOL) over 13 years of follow-up. Patients with FD experience multiorgan dysfunction and ...

Fabry disease is a progressive condition that can come with a complex range of symptoms and complications that includes neuropathic pain, skin manifestations, and gastrointestinal issues. If left ...

Dublin, July 18, 2025 (GLOBE NEWSWIRE) -- The "Fabry Disease Market (By Treatment, Route of Administration, Product, End-User, Country Analysis), Key Company Profiles, Product Portfolio, Pipeline ...

Drug shortage led to kidney disease and stroke reports. Oct. 28, 2011— -- Hundreds of Fabry disease patients sickened because of a U.S. shortage of a drug that keeps them alive are hopeful they ...

Please provide your email address to receive an email when new articles are posted on . Nephrologists often see patients with common or well-known conditions, including kidney stones, diabetes, high ...

Background. A 29-year-old white woman with a family history of Fabry disease was referred to a nephrology clinic with hypertension and nephropathy. Her renal function was below normal (serum ...

Fabry disease is a rare condition that can run in families. The symptoms can vary from person to person, including pain or tingling in the hands and feet and a type of rash. If you are suffering from ...