A new gene-targeting strategy that boosts a crucial brain protein could pave the way for the first effective treatment for ...
Valentina Torres' parents hope that in the future she will be able to walk and "not be trapped inside her own body".
A team of researchers at Texas Children's Duncan Neurological Research Institute (NRI) and Baylor College of Medicine report ...
A team of researchers at Baylor College of Medicine and the Duncan Neurological Research Institute (Duncan NRI) at Texas ...
Researchers have discovered a new way to increase a key brain protein damaged in Rett syndrome, a rare genetic disorder that affects thousands of children worldwide. Early studies in mice and ...
A mum has given an insight into her daughter’s life, who is left locked in her body due to a “devastating” rare condition.