We hold leadership positions in Duchenne muscular dystrophy (Duchenne) and limb-girdle muscular dystrophies (LGMDs) and are building a robust portfolio of programs across muscle, central nervous ...

Edgewise Therapeutics Announces Expansion of their EDG-5506 Clinical Program in Duchenne Muscular Dystrophy (Duchenne) – Initiating new Phase 2 FOX trial in boys with Duchenne who have been ...

hC Bioscience Announces Program in Duchenne Muscular Dystrophy and Reports In Vivo Data From tRNA-based Protein Editing PlatformMay 24, 2024 – Boston, Mass. — hC Bioscience, a ...

University of Manchester scientists have mapped the mutations in the tiny protein chains that cause a subtype of muscular ...

Tomorrow’s opportunity. Join for Free » Sarepta Therapeutics Announces Pipeline Progress for Multiple Limb-Girdle Muscular Dystrophy Programs Apr. 15, 2025 8:30 AM ET Sarepta Therapeutics, Inc ...